Rare Diseases & Orphan Drugs
Rare diseases affect a small percentage of the population, often presenting unique challenges in diagnosis and treatment. Orphan drugs are specialized medications designed to prevent, diagnose, or treat these conditions. Due to limited patient numbers, developing treatments for rare diseases can be complex and costly. However, advancements in genomics, biotechnology, and personalized medicine have accelerated orphan drug development. Regulatory incentives, such as market exclusivity and financial support, have further encouraged research in this area. By addressing unmet medical needs, orphan drugs offer hope to patients with rare conditions, significantly improving quality of life and enhancing healthcare outcomes.
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Rare Diseases & Orphan Drugs Conference Speakers
Recommended Sessions
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